Article
Treatment with Ataluren for Duchene Muscular Dystrophy
Pediatr Neurol Briefs
Publication/Presentation Date
12-4-2020
Abstract
Investigators from Europe and the USA, representing the STRIDE Registry and Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS), examined the effectiveness of ataluren and standard of care in the Registry versus stand of care alone in the CINRG DNHS.
Disciplines
PubMedID
33304086
Peer Reviewed for front end display
Peer-Reviewed
Document Type
Article
Citation Information
Morkous S. S. (2020). Treatment with Ataluren for Duchene Muscular Dystrophy. Pediatric neurology briefs, 34, 12. https://doi.org/10.15844/pedneurbriefs-34-12