"Treatment with Ataluren for Duchene Muscular Dystrophy" by Sameh S Morkous, MD, FAAN

Selected Works of Sameh Morkous, MD, FAAP, FAAN, FAASM

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Treatment with Ataluren for Duchene Muscular Dystrophy

Pediatr Neurol Briefs

Sameh S Morkous, MD, FAAN, Lehigh Valley Health Network

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Publication/Presentation Date

12-4-2020

Abstract

Investigators from Europe and the USA, representing the STRIDE Registry and Cooperative International Neuromuscular Research Group (CINRG) Duchenne Natural History Study (DNHS), examined the effectiveness of ataluren and standard of care in the Registry versus stand of care alone in the CINRG DNHS.

Disciplines

Medicine and Health Sciences and
Pediatrics

PubMedID

33304086

Peer Reviewed for front end display

Peer-Reviewed

Document Type

Article

Citation Information

Morkous S. S. (2020). Treatment with Ataluren for Duchene Muscular Dystrophy. Pediatric neurology briefs, 34, 12. https://doi.org/10.15844/pedneurbriefs-34-12