About Christian Mueller
Cystic Fibrosis (15)
Cystic fibrosis transmembrane conductance regulator deficiency exacerbates islet cell dysfunction ...
Pulmonary and Allergy (2006)
The cause of cystic fibrosis-related diabetes (CFRD) remains unknown, but cystic fibrosis transmembrane conductance regulator (CFTR) mutations contribute directly to ...
alpha 1-Antitrypsin Deficiency (10)
Human Treg responses allow sustained recombinant adeno-associated virus-mediated transgene expression
University of Massachusetts Medical School Faculty Publications (2013)
Recombinant adeno-associated virus (rAAV) vectors have shown promise for the treatment of several diseases; however, immune-mediated elimination of transduced cells ...
rAAV9 airway delivery results in effective knockdown of mutant alpha ...
UMass Center for Clinical and Translational Science Research Retreat (2012)
Alpha 1-Antitrypsin (AAT) deficiency is a human genetic disease resulting in the production of mutant AAT, a hepatocyte produced serine ...